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International Registry of Dravet Syndrome and other Syndromes correlated with genes on SCN1A and PCDH19

Gait deviations in patients with dravet syndrome: A systematic review. - PubMed - NCBI https://www.ncbi.nlm.nih.gov/pubmed/30940509
Eur J Paediatr Neurol. 2019 Mar 22. pii: S1090-3798(18)30548-8. doi: 10.1016/j.ejpn.2019.03.003. [Epub ahead of print] Review
Dravet syndrome gene therapy http://www.draccon.com/dracaena-report/2019/2/25/dravet-syndrome-gene-therapy
There are multiple gene therapy programs in development for Dravet syndrome including those that supply and extra copy of the SCN1A gene and those that boost expression from the healthy SCN1A gene copy. Clinical trials are around the corner, ...

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